SMA Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
15,934Targets
453Trials
84Drugs
7Datasets
7,947Sources
226,991Claims
263,546Evidence
58,010Hypotheses
DRUGpreclinicalsmall molecule

chembl1466254

Mechanism

toluamide-piperidine-morpholine; SMN1/SMN2 binder pchembl=8.66, BBB=0.97

Structure

Cc1ccccc1C(=O)NC1CCN(C(=O)N2CCOCC2)CC1

Related claims (0)

No claims matched “chembl1466254” in free-text search.

Off-Target Findings (0)

No Boltz-2 / Chai-1 off-target panel claims recorded for this drug.

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