SMA Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
15,934Targets
453Trials
84Drugs
7Datasets
7,947Sources
226,991Claims
263,546Evidence
58,010Hypotheses
DRUGapprovedsmall molecule

ziconotide

Approved indications

severe-chronic-pain-intrathecal

Related claims (0)

No claims matched “ziconotide” in free-text search.

Off-Target Findings (17)

T1: 1T4: 4untiered: 12
TargetRoleTierBoltz-2 iPTMChai-1 iPTMVerdict
STMN1SMAT10.588Primary SMA hit
CHRNA1_ECDOTHERT40.897Low relevance
HSP70_NBDOTHERT40.815Low relevance
KCNA2_poreOTHERT40.592Low relevance
CHRNG_fetalOTHERT40.556Low relevance
EIF4E_capbindingUNCLASSIFIED0.834
LRP4_propellerOTHER0.776
LIMK2_aCOTHER0.750
RIPK3_kinaseUNCLASSIFIED0.623
RAPSN_ntermOTHER0.622
MLKL_4HBUNCLASSIFIED0.619
PERP_ECL1OTHER0.608
S100B_dimerUNCLASSIFIED0.598
PFN2SMA0.583
PLS3_EF4OTHER0.467
AQP4_M1UNCLASSIFIED0.458
KEAP1_KELCHUNCLASSIFIED0.404
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